Also mentions FDA:
Document clustering based on entity association rules
x hide permanently

Opportunities for developing therapies for rare genetic diseases: focus on gain-of-function and allostery.

NCBI HomePage

Opportunities for developing therapies for rare genetic diseases: focus on gain-of-function and allostery.

Orphanet J Rare Dis. 2017 Apr 17;12(1):61

Authors: Chen B, Altman RB

Abstract BACKGROUND: Advances in next generation sequencing technologies have revolutionized our ability to discover the causes of rare genetic diseases. However, developing treatments for these diseases remains challenging.

Mentions: FDA